Spinal muscular atrophy (SMA) impacts individuals across a range of ages — from infants and children to teens and adults — with varying levels of severity. For nearly a decade, innovations have greatly improved outcomes for people living with SMA, like Nathan, but important unmet needs remain. Our commitment to advancing research that addresses these gaps is unwavering. Learn more about Nathan’s story and our work in SMA: https://ow.ly/K90x50TKSh4 | Biogen
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Spinal muscular atrophy (SMA) impacts individuals across a rang…
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New detailed findings highlight the potential of an investigational form of our spinal muscular atrophy (SMA) therapy. These data will be presented in a session at the Annual Congress of the World Muscle Society by Thomas Crawford, M.D., co-director, Muscular Dystrophy Association Clinic at Johns Hopkins Medicine. Learn more about our latest research: https://ow.ly/QqlX50THSXX | Biogen
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Animation depicting a novel new Gene Therapy treatment modifying a mutated gene to prevent cancer .
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Today, the Food and Drug Administration approved a new gene therapy for Spinal Muscular Atrophy. SMA Type 1 is the number one genetic killer of children 2 and under. This first-time gene therapy, developed here at Nationwide Children's, is allowing kids like Evelyn to have a bright future. Watch her incredible story. | Nationwide Children's Hospital
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How does gene therapy work? 🧬 with Dr Karl Kruszelnicki #GreatMomentsInScience #GeneTherapy #SMA #SpinalMuscularAtrophy #Science | ABC Science
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If Hannah has the SMA gene, there is a chance our kids will have SMA. If she doesn't, there's no chance. 🧬 | Squirmy and Grubs
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